index - Thérapie génique pour la DMD & physiopathologie du muscle squelettique

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Ex-vivo Homeostasis CaV subunits CaVβs LKB1 Epigenetics Diseases Dystrophie musculaire de Becker Long noncoding RNA DMD Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Muscular dystrophy Metabolism Mitochondrial fission Muscle Strength Knockout Base Sequence Human Umbilical Vein Endothelial Cells Becker muscular dystrophy BMD Inbred C57BL Inhibitors Gene Expression Regulation/drug effects Cultured Autophagy Myotendinous junction Muscular Dystrophy Morphogenesis CD38 Cardiomyopathy Humans Centronuclear myopathy Muscle Biology Mice Muscles/physiopathology Cachexia BMD Dystrophin central domain Muscle development Cardiomyopathie DMO Clinical trials Duchenne muscular dystrophy DMD Dystrophie Musculaire de Duchenne DMD Dystrophy Calcium Activin Receptors Invivo Myogenesis Calcium Channels MES Multi exon skipping Allele‐specific silencing therapy LncRNA Immunoglobulin Fc Fragments/pharmacology Dystrophin Becker muscular dystrophy DHPR α1S Animals MiARN Muscle Génomique Multi resolution modeling Male Molecular Sequence Data Dystrophie Musculaire de Becker BMD Dystrophin-EGFP NAD+ Delivery Molecular docking Dynamin 2 Becker BMD muscular dystrophy NNOS Cell homeostasis Skeletal muscle Muscular Atrophy L-Type Duchenne DMD dystrophy Exon skipping Cell Line Genomic Hear Multiresolution modeling Cells Gene expression Cell Biology Hepatocellular carcinoma CTNNB1 Duchenne muscular dystrophy Inbred mdx Gene modifiers Drp1 Energy Metabolism/drug effects Long QT Antisense oligonucleotides Dystrophine LncARN Modificateurs de gènes Mdx mouse Liver Animal/physiopathology